Delivering the hope of

genetic medicine to patients

with rare diseases


We’re harnessing the body’s natural DNA repair

process to provide precise, stable and durable

therapies to patients with serious genetic

diseases

Delivering the hope of

genetic medicine to patients with rare diseases

We’re harnessing the body’s natural DNA repair process to provide precise, stable and durable therapies to patients with serious genetic diseases

Pioneering a safer, site-specific genome-editing technology


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