Delivering the hope of genetic medicine to patients with rare diseases

We’re harnessing the body’s natural DNA repair process to provide precise, stable and durable therapies to patients with serious genetic diseases

Delivering the hope of genetic medicine to patients with rare diseases

We’re harnessing the body’s natural DNA repair process to provide precise, stable and durable therapies to patients with serious genetic diseases

Pioneering a safer, site-specific genome-editing technology

Learn about GeneRide™

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