Delivering the hope of genetic medicine to patients with rare diseases
We’re harnessing the body’s natural DNA repair process to provide precise, stable and durable therapies to patients with serious genetic diseases
Delivering the hope of genetic medicine to patients with rare diseases
We’re harnessing the body’s natural DNA repair process to provide precise, stable and durable therapies to patients with serious genetic diseases
Dedicated to providing one-time treatments with durable results
Committed to improving the lives of young patients
Making rapid progress toward our goal of helping patients
Pioneering a safer, site-specific genome-editing technology
Learn about GeneRide™